Overview
Research studies and clinical trials are carefully designed to evaluate the safety and effectiveness of potential treatments. Gene therapy clinical trials for cardiomyopathy provide patients the possibility of access to an investigational treatment and the ability to contribute to the advancement of scientific research that may also help other individuals with the disease.
- To learn more about Gene Therapy Clinical Trials and how they work, click here.
- See below to access listings of CURRENT Gene Therapy Research Studies and Clinical Trials.
Current Genetic Cardiomyopathy Clinical Trials
Current gene therapy clinical trials for cardiomyopathy:
- Lexeo/PKP2
- Tenaya/MYBPC3
For a more complete listing of genetic cardiomyopathy research studies and clinical trials, please visit www.clinicaltrials.gov.
There, you will find a search tool that allows you to search current clinical trials available for your condition. (See sample search tool instructions and image below.)
Please follow these instructions to use the search tool:
- In the box labeled “Condition/disease”, simply type in “cardiomyopathy.”
- Alternatively, you can type in “DCM”, “HCM”, or “ARVC”.
- You can also type in your specific gene mutation to locate clinical trials associated with your gene.
- Or, if you know the trial’s “NCT” number, you can enter it and you will be taken directly to that trial page.
- In the box labeled “Other terms” you can also type in a company name if you know of a company doing a clinical trial in your disease area. Or, you can type in the name of a particular study drug, or any other term that will help define your search.
- Location: Initially, we recommend leaving the location field blank.
You may be surprised at the number of clinical trials currently underway for various types of genetic cardiomyopathy. This tool allows you to be more selective in how you search. Please use the filters to narrow search results to those trials that may best suit your particular situation.